【Intractable, Rare or Refractory diseases】 Details of the Research Topics

We invite your proposals for collaborative research relating to drug candidates (low-molecular compounds, peptides, nucleic acids, gene therapy, etc.) for intractable, rare or refractory diseases. We also welcome your proposals for collaborative research regarding drug targets for nucleic acid medicines.

Interest diseases

  • Intractable diseases and rare diseases.
  • Diseases caused by single gene mutations or diseases with clear drug discovery targets and causative genes.
  • Refractory diseases with a high unmet medical need.
  • Refractory diseases in obstetrics and gynecology, gastroenterology, dermatology, or orthopedic, etc.
  • Excluding cancer and ophthalmologic diseases.

Research topics

  • Drug candidates that lead to curative therapy, not symptomatic.
  • Drug candidates that induce or promote regenerative (repair) action in the body.
  • Drug candidates based on nucleic acid, peptide, gene therapy.
  • Drug targets for nucleic acid medicine for treatment of intractable, rare or refractory diseases.